Tag: rare diseases
CRISPR and other new technologies open doors for drug development, but...
C. Michael White, University of Connecticut
Prescription drugs and vaccines revolutionized health care, dramatically decreasing death from disease and...
Flesh-eating bacteria infections are on the rise in the US −...
Bill Sullivan, Indiana University
Flesh-eating bacteria sounds like the premise of a bad horror movie, but it’s a growing...
Celine Dion’s diagnosis of stiff-person syndrome brought a rare neurological diagnosis...
Bhavana Patel, University of Florida and Torge Rempe, University of Florida
The announcement by celebrated singer Celine Dion in...
First gene therapy for Tay-Sachs disease successfully given to two children
Miguel Sena-Esteves, UMass Chan Medical School
Two babies have received the first-ever gene therapy for Tay-Sachs disease after over...